09:00 – 12:00:
Physiotherapist and Investigator Training Workshop
Core dataset – adults (DM1 and DM2) and pediatrics (Kate Eichinger)
Topics:
13:00 – 14:00:
Lunch buffet
14:00 – 16:00:
Cognitive Training Workshop
Core dataset – adults and pediatrics
17:00 – 17:15:
Opening Session
(Valeria Sansone, Guillaume Bassez, Benedikt Schoser)
17:15 – 17:45:
Define the Meeting Objectives – Start-up Activities – Part I
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17:45 – 19.40:
Scientific talks: Translational and Clinical Insights in Myotonic Dystrophy
Moderator: Chris Turner, Stefan Winblad
20:30:
Networking dinner
08:30 – 10.00:
Start-up Activities – Part II
(Valeria Sansone, Benedikt Schoser)
10.00 – 11.15:
Scientific talks: Registry Updates and Clinical Research Developments in Myotonic Dystrophies:
Moderators: Peter Bram ‘t Hoen, Roberto Massa
11.15 – 11.30:
Coffee Break
11.30-13.10:
Scientific talks: Global Insights and Collaborative Advances in DM
Moderators: Nicholas E. Johnson, Gabriella Silvestri
13.00-14.00
Working Lunch
14.00-16.00
Stakeholders Perspective Session – Bridging the Gap for Clinical Site Preparedness
Moderators: Benedikt Schoser, Guillaume Bassez
14:00 – 14:30 – Patients’ Organization: What is the role of the patients? (Andy Rohwasser, Baas Haasakker, Jorg van Gent)
14:30 – 15:00 – Site Readiness: Clinician Perspective (Valeria Sansone)
15:00 – 16:00 – Round table: Ask the Industry – Gaining Insights and Perspectives (Allison Kreuzer, Fares Nigim, Johan van Beek, Julia Presanis, Alla Zozulya Weidenfeller)
16:00 – 17:00:
Wrap-up & Next Steps & Meeting (Scientific Committee)
